DEPARTMENT OF DEFENSE - CONGRESSIONALLY DIRECTED MEDICAL RESEARCH PROGRAMS

Vision - To extend and improve the function, quality of life, and life span for all individuals diagnosed with DMD

Duchenne Muscular Dystrophy Program Cover Image

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Duchenne muscular dystrophy (DMD) affects approximately 1 out of every 3,500 male infants (about 20,000 new cases a year). This form of muscular dystrophy results from mutations in the dystrophin gene that lead to an absence of dystrophin in muscle cells, allowing these cells to be easily damaged. Boys living with DMD experience devastating muscle weakness that affects the skeletal muscles, heart, and respiratory muscles. Symptoms of DMD typically develop prior to age 5, and by age 12 most patients are confined to a wheelchair. Currently, there is no cure for DMD and young men with this disease rarely live beyond their early 30s. Over the past several years, research has identified many novel therapeutic targets and significantly expanded the number of potential therapeutics in the pipeline for DMD. The DMDRP aims to accelerate the transformation of these promising therapeutic ideas into clinical applications and support the training of new physician researchers to encourage careers in DMD research.



Congressional Appropriations

Congressional Appropriations

  • $13.6 million
    FY11-FY14
  • $3.2 million
    FY15

Funding Summary

Funding
Summary


Muscular Dystrophy Coordinating Committee (MDCC)

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Vision

To extend and improve the function, quality of life, and life span for all individuals diagnosed with DMD

Mission

To better inform the development of drugs, devices, and other interventions and promote their effective clinical testing.


Last updated Friday February 05 2016